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LEZIONE terapia genica pdf - Universita degli studi di Ferrara

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PTC124 (gentamicin analogue): read through premature<br />

termination codons<br />

PTC124 targets genetic <strong>di</strong>sorders caused by nonsense<br />

mutations (Nature, 2007)<br />

PTC124: it may correct nonsense mutations<br />

only

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