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LEZIONE terapia genica pdf - Universita degli studi di Ferrara

LEZIONE terapia genica pdf - Universita degli studi di Ferrara

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Terapia cellulare<br />

Trapianti cellulari<br />

Trapianto cellule staminali geneticamente mo<strong>di</strong>ficate ex-vivo<br />

SUCCESSI<br />

ADA-SCID, Aiuti, 2002<br />

X-SCID, Hacein-Bey-Abina, 2002<br />

Epidermolisi bullosa, De Luca, 1998<br />

Ferite epidermide, Quesenberry, 2002<br />

POTENZIALITA’<br />

Malattie metaboliche<br />

Malattie ematologiche<br />

M. Parkinson<br />

M. <strong>di</strong> Alzheimer<br />

Infarto<br />

Diabete<br />

Artrite reumatoide

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