FINAL PROGR AM - American Society of Gene & Cell Therapy
FINAL PROGR AM - American Society of Gene & Cell Therapy
FINAL PROGR AM - American Society of Gene & Cell Therapy
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<strong>AM</strong>ERICAN SOCIETY OF GENE THERAPY • Final Program 61<br />
ABSTRACTS<br />
THURSDAY, JUNE 2<br />
Muscle and Connective Tissue: <strong>Gene</strong> <strong>Therapy</strong> for<br />
Muscular Dystrophy<br />
251<br />
Dystrophin in Vascular Smooth Muscle Is Important for<br />
Duchenne Muscular Dystrophy <strong>Therapy</strong><br />
Kaori Ito, Shigemi Kimura, Gail D. Thomas, Shiro Ozasa,<br />
Makoto Matsukura, Makoto Ikezawa, Hiroe Ueno, Kowashi<br />
Yoshioka, Misao Suzuki, Takeshi Miwa Teruhisa Miike<br />
252<br />
A Novel Approach <strong>of</strong> Gentamicin <strong>Therapy</strong> for Duchenne<br />
Muscular Dystrophy Using Hybrid Liposome and<br />
Establishment <strong>of</strong> a System To Identify the Patients<br />
Eligible for the Treatment<br />
Shigemi Kimura, Kaori Ito, Shro Ozasa, Hiroe Kawano,<br />
Makoto Ikezawa, Makoto Matsukura, Ryuichi Ueoka, Yoko<br />
Matsumoto, Msafumi Matsuo, Yasuhiro Takeshima Teruhisa<br />
Miike<br />
253<br />
An AAV Vector-Mediated <strong>Gene</strong> Transfer into Canine<br />
Skeletal Muscle<br />
Madoka Ikemoto, Katsutoshi Yuasa, Madoka Yoshimura, Akiyo<br />
Nishiyama, Yuko Miyagoe-Suzuki, John McC Howell,<br />
Shin’ichi Takeda<br />
254<br />
Decorin Promotes Differentiation <strong>of</strong> Myoblasts into<br />
Myotubes That Express Slow MyHC In Vitro<br />
Yong Li, Juan Li, Ying Tang, Xiao Xiao, Johnny Huard<br />
255<br />
Embryonic Stem <strong>Cell</strong>-Mediated Regenerative <strong>Therapy</strong><br />
for Duchenne Muscular Dystrophy<br />
Shiro Ozasa, Shigemi Kimura, Makoto Matsukura, Kaori Ito,<br />
Makoto Ikezawa, Hiroe Kawano, Teruhisa Miike, Kenichi<br />
Yamamura, Kimi Araki, Kuniya Abe Hitoshi Niwa<br />
256<br />
An Ideal Therapeutic Agent for Duchenne Muscular<br />
Dystrophy Involving a Gutted Adenovirus Expressing<br />
Full-Length Utrophin<br />
Jatinderpal R. Deol, Renald Gilbert, Mylene Bourget, Joon-Shik<br />
Moon, Josephine Nalbantoglu, George Karpati<br />
257<br />
Ex Vivo <strong>Gene</strong> <strong>Therapy</strong> for Duchenne Muscular Dystrophy:<br />
Lentiviral and PhiC31 Integrase Approaches<br />
Simon P. Quenneville, Pierre Chapdelaine, Joël Rousseau,<br />
Michele P. Calos, Jacques P. Tremblay<br />
258<br />
Identification <strong>of</strong> Differentially Expressed <strong>Gene</strong>s in<br />
Duchenne Muscular Dystropy Utilising RNAi Technology:<br />
Possible Targets for <strong>Gene</strong> <strong>Therapy</strong><br />
Mohammad Mahdi Ghahramani Seno, Ian R. Graham, Ken<br />
Laing, Marita Pohlschmidt, Takis Athanasopoulos, Mark<br />
Crompton, George J. Dickson<br />
259<br />
Uterine Fibroids <strong>Gene</strong> <strong>Therapy</strong>: Adenovirus-Mediated<br />
Herpes Simplex Virus Thymidine Kinase/Ganciclovir<br />
Treatment Inhibits Growth <strong>of</strong> Human and Rat Leiomyoma<br />
<strong>Cell</strong>s<br />
Ayman Al-Hendy, Marwa Kamel, Gregory Christman, Salama<br />
A. Salama<br />
260<br />
A Database for Managing Neuromuscular Disease Data<br />
in the Province <strong>of</strong> Quebec<br />
Charland Luc, Lavoie Jeremie, Puymirat Jack<br />
261<br />
Recombinant Adeno-Associated Viral (rAAV)<br />
Microdystrophin Vectors as Therapeutic Tools for<br />
Duchenne Muscular Dystrophy (DMD)<br />
Takis Athanasopoulos, Ian Graham, Helen Foster, Norma Perez,<br />
Adeline Vulin, Vanessa Hill, Stewart Fabb, Luis Garcia, Olivier<br />
Danos, George Dickson<br />
262<br />
Plasmid-Mediated <strong>Gene</strong> Transfer in mdx Mice Using<br />
Mini- and Micro-Dystrophin Constructs<br />
Leland E. Lim, Carmen Bertoni, Thomas A. Rando<br />
263<br />
Characterization and <strong>Gene</strong> Transfer in Mesenchymal<br />
Stem <strong>Cell</strong>s Derived from Human Umbilical Cord Blood<br />
Feizhou Lu, Jianyuan Jiang, Masayuki Fujino, Xiao-Kang Li<br />
264<br />
<strong>Cell</strong> <strong>Therapy</strong> <strong>of</strong> Ovarian Failure: Intraovarian Transplanted<br />
Granulosa <strong>Cell</strong>s Successfully Engraft and Repopulate<br />
Growing Follicles<br />
Ayman Al-Hendy, Hui Q. Wang, Salama A. Salama<br />
265<br />
Enhanced Plasmid-Mediated Dystrophin Expression in<br />
the mdx Mouse Model for Duchenne Muscular Dystrophy<br />
by a PhiC31 Integrase Plasmid System<br />
Carmen Bertoni, Sohail Jarrahian, Thurman M. Wheeler,<br />
Yining Li, Eric C. Olivares, Michele P. Calos, Thomas A.<br />
Rando<br />
266<br />
Development <strong>of</strong> rAAV-Based Skeletal and Cardiac<br />
Muscle Regulatory Cassettes for <strong>Gene</strong> <strong>Therapy</strong> <strong>of</strong><br />
Duchenne Muscular Dystrophy<br />
Maja Z. Salva, Charis L. Himeda, Phillip Tai, Michael J.<br />
Blankinship, Paul Gregorevic, James M. Allen, Leonard A.<br />
Meuse, Jeffrey S. Chamberlain, Stephen D. Hauschka
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