FINAL PROGR AM - American Society of Gene & Cell Therapy
FINAL PROGR AM - American Society of Gene & Cell Therapy
FINAL PROGR AM - American Society of Gene & Cell Therapy
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30<br />
8th Annual Meeting • June 1 - 5, 2005 • St. Louis<br />
SCIENTIFIC <strong>PROGR</strong><strong>AM</strong><br />
THURSDAY, JUNE 2, 2005<br />
Workshop 211<br />
<strong>Gene</strong>-Based Vaccines: New Developments for <strong>Gene</strong>tic<br />
Vaccines<br />
Room: 120/124<br />
Chair: David B. Weiner, PhD<br />
Speakers: Richard Heller, PhD - Electroporation Mediated<br />
Immunotherapy <strong>of</strong> Solid Tumors: Preclinical<br />
Results and Initiation <strong>of</strong> Clinical Study<br />
Leaf Huang, PhD - LPD Nanoparticles: A<br />
<strong>Gene</strong> Vector Turned into a Potent Vaccine Carrier<br />
David B. Weiner, PhD - Expanding the Potency<br />
and Breadth <strong>of</strong> the Immune Responses Induced by<br />
DNA Vaccines<br />
Britta Elisabeth Wahren, MD, PhD - Means to<br />
Induce Mucosal Immunity in HIV <strong>Gene</strong>tic<br />
Immunization<br />
Ning-Sun Yang, PhD - Developing Multiple<br />
Viral Protein <strong>Gene</strong>s and Virus-like Particles as<br />
<strong>Gene</strong>-based Vaccines<br />
Workshop 212<br />
Hemopoietic: Hemopoietic Stem <strong>Cell</strong> <strong>Gene</strong> <strong>Therapy</strong><br />
Room: Ferrara Theater<br />
Chair: Jan Nolta, PhD<br />
Speakers: Carolyn Wilson, PhD - Addressing Safety<br />
Concerns for Hematopoietic Stem <strong>Cell</strong> <strong>Gene</strong><br />
<strong>Therapy</strong> - A FDA Perspective<br />
Manuel Grez, PhD - Correction <strong>of</strong> Chronic<br />
Granulomatous Disease by <strong>Gene</strong> <strong>Therapy</strong><br />
Marina Cavazzana-Calvo, MD, PhD -<br />
Clinical and Biological Results from the SCID-XI<br />
<strong>Gene</strong> <strong>Therapy</strong> Trial<br />
Stanton L. Gerson, MD - In Vivo Stem <strong>Cell</strong><br />
Selection without Myeloablation<br />
Alessandro Aiuti, MD, PhD - <strong>Gene</strong> <strong>Therapy</strong> <strong>of</strong><br />
ADA-deficient SCID<br />
Workshop 213<br />
Immunology <strong>of</strong> <strong>Gene</strong> <strong>Therapy</strong>: Organ<br />
Specific Immunity<br />
Room: 260/264<br />
Chair: Roland W. Herzog, PhD<br />
Speakers: Pedro Lowenstein, MD, PhD - Immune<br />
Responses to Viral Vectors in the Central Nervous<br />
System<br />
John Iacomini, PhD - Reshaping the Immune<br />
System Using <strong>Gene</strong> <strong>Therapy</strong><br />
Roland W. Herzog, PhD - In Vivo <strong>Gene</strong><br />
Transfer to Liver and Muscle; Two Organs, Two<br />
Different Stories<br />
Hans-Peter Kiem, MD - Immune Responses to<br />
<strong>Gene</strong>-modified Hematopoietic <strong>Cell</strong>s<br />
Workshop 214<br />
Industrial Liaison: Pre-Clinical Issues in <strong>Gene</strong> <strong>Therapy</strong><br />
Room: 263/267<br />
Chair: Douglas J. Jolly, PhD<br />
Speakers: Rebecca Sheets, PhD - Pre-clinical<br />
Development <strong>of</strong> Adenovirus-vectored HIV Vaccine<br />
Candidate<br />
Joy Cavagnaro, PhD, DABT, RAC -<br />
Optimizing Design and Analysis <strong>of</strong> Preclinical<br />
Development Programs<br />
Boro Dropulic, PhD - Clinical Translation <strong>of</strong> a<br />
Lentiviral Vector for the Treatment <strong>of</strong> HIV/AIDS<br />
Peter K. Working, PhD, DABT - Preclinical<br />
Strategies: Taking an “Armed” Oncolytic<br />
Adenovirus to the Clinic<br />
Workshop 215<br />
Programs <strong>of</strong> Excellence in <strong>Gene</strong> <strong>Therapy</strong><br />
Room: 230/231<br />
Chair: Sonia I. Skarlatos, PhD<br />
Speakers: Sonia I. Skarlatos, PhD - PEGT Overview<br />
Haig H. Kazazian, Jr., MD - Preclinical <strong>Gene</strong><br />
<strong>Therapy</strong> <strong>of</strong> Hemophilia A with New AAV<br />
Serotypes<br />
Ronald G. Crystal, MD - <strong>Gene</strong> therapy for<br />
Alpha 1-antitrypsin Deficiency with Intrapleural<br />
Administration <strong>of</strong> Novel AAV Serotypes<br />
Barry London, MD, PhD - <strong>Gene</strong> <strong>Therapy</strong><br />
During LVAD Support: Can We Fix the Broken<br />
Heart?<br />
Stanley Riddell, MD - Regulating T cells for<br />
Immunotherapy by <strong>Gene</strong> Insertion<br />
Richard A. Knazek, MD - The National <strong>Gene</strong><br />
Vector Laboratories - Production, Toxicology,<br />
Repository, Clonality Testing and Long-Term<br />
Follow Up<br />
Workshop 216<br />
Respiratory Tract: What’s New in Animal Models for<br />
Lung <strong>Gene</strong> <strong>Therapy</strong><br />
Room: 265/266<br />
Chair: Stephen Hyde, PhD<br />
Speakers: Bruce Bunnell, PhD - Mouse or Monkey: What<br />
is the FDA Looking for in Pre-clinical Data?<br />
Alice F. Tarantal, PhD - Monkey Model for Fetal<br />
Intrapulmonary <strong>Gene</strong> Transfer<br />
John F. Engelhardt, PhD - Are Men Mice or<br />
Pigs? A Lung <strong>Gene</strong> <strong>Therapy</strong> and <strong>Cell</strong> Biology<br />
Perspective<br />
Uta Griesenbach, PhD - FABp-CF Knockout<br />
Mice as Models for CFTR <strong>Gene</strong> Transfer<br />
Gerry McLachlan, PhD - Evaluation Non-viral<br />
<strong>Gene</strong> Transfer in the Ovine Lung