FINAL PROGR AM - American Society of Gene & Cell Therapy
FINAL PROGR AM - American Society of Gene & Cell Therapy
FINAL PROGR AM - American Society of Gene & Cell Therapy
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<strong>AM</strong>ERICAN SOCIETY OF GENE THERAPY • Final Program 13<br />
RESEARCH AWARDS AND TRAVEL GRANT RECIPIENTS<br />
EXCELLENCE IN RESEARCH AWARDS<br />
For Students and Postdoctoral Fellows<br />
Alessandra Biffi – Postdoctoral Fellow<br />
Cure <strong>of</strong> Established Disease and Direct Evidence <strong>of</strong> <strong>Cell</strong>ular<br />
Cross-Correction in the Nervous System <strong>of</strong> Metachromatic<br />
Leukodystrophy Mice after HSC-Based <strong>Gene</strong> <strong>Therapy</strong><br />
Katherine Bowman – Student<br />
Oral Delivery <strong>of</strong> Non-Viral DNA Nanoparticles for<br />
Hemophilia A<br />
*Li Chen – Postdoctoral Fellow<br />
Complete and Persistent Phenotypic Correction <strong>of</strong> Phenylketonuria<br />
in Mice by Site-Specific Genome Integration <strong>of</strong><br />
Phenylalanine Hydorxylase cDNA<br />
Aurelie Goyenvalle – Student<br />
Highly Efficient Exon-Skipping and Sustained Correction <strong>of</strong><br />
Muscular Dystrophy Using an Adeno-Associated Viral Vector<br />
*Fanconi Anemia Research Fund Recipient<br />
TRAVEL GRANT RECIPIENTS<br />
For Students and Postdoctoral Fellows<br />
George Aslanidi<br />
Alessandra Biffi<br />
Martina Blumenthal<br />
Katherine Bowman<br />
Jian Chen<br />
Li Chen<br />
Hu Dai<br />
Mo Dao<br />
Michele De Palma<br />
Hongzhe Duan<br />
Anja Ehrhardt<br />
Herena Eixarch<br />
Anuj Gaggar<br />
Sabine Gerull<br />
Debadyuti R. Ghosh<br />
Aurelie Goyenvalle<br />
Jaeseok Han<br />
Scott Q. Harper<br />
Anne Kiang<br />
Changlong Li<br />
Jaeseok Han – Student<br />
Glucose-Dependent Insulin Production by Liver-Specific,<br />
Glucose-Regulatable Synthetic Promoters Results in the Cure<br />
<strong>of</strong> Diabetes<br />
Anne Kiang – Student<br />
Complement Blockade Prevents Several Innate Toxicities<br />
Rapidly Induced after Intravenous Adenovirus (Ad) Vector<br />
Administration<br />
Ruth Seggewiss – Postdoctoral Fellow<br />
Myeloid Sarcoma Associated with <strong>Gene</strong> Marking <strong>of</strong><br />
Hematopoietic Stem <strong>Cell</strong>s in a Rhesus Macaque<br />
Yan Shou – Postdoctoral Fellow<br />
Mouse Models for the Analysis <strong>of</strong> <strong>Gene</strong>tic Risk Factors for<br />
Hematopoietic Transformation in XSCID <strong>Gene</strong> <strong>Therapy</strong><br />
Angelo Leone Lombardo<br />
Francesco Marangoni<br />
Robert A. Marr<br />
Joel Montane<br />
John R. Ohlfest<br />
Cedric Raoul<br />
Luis Sanchez-Perez<br />
Manfred Schmidt<br />
Kerstin Schwarzwaelder<br />
Ruth Seggewiss<br />
Yan Shou<br />
Yue Si<br />
Matthias Stephan<br />
Konrad L. Streetz<br />
Yuki Takahashi<br />
Uma Thanarajasingam<br />
Zhijian Wu<br />
Tom Wurdinger<br />
Fang Xu<br />
Xiao-Bing Zhang<br />
The Excellence in Research Awards and Travel Grants were made possible<br />
through grant support from